Search results for "Respiratory system abnormalitie"

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The oculoauriculofrontonasal syndrome: Further clinical characterization and additional evidence suggesting a nontraditional mode of inheritance

2018

IF 2.264; International audience; The oculoauriculofrontonasal syndrome (OAFNS) is a rare disorder characterized by the association of frontonasal dysplasia (widely spaced eyes, facial cleft, and nose abnormalities) and oculo-auriculo-vertebral spectrum (OAVS)-associated features, such as preauricular ear tags, ear dysplasia, mandibular asymmetry, epibulbar dermoids, eyelid coloboma, and costovertebral anomalies. The etiology is unknown so far. This work aimed to identify molecular bases for the OAFNS. Among a cohort of 130 patients with frontonasal dysplasia, accurate phenotyping identified 18 individuals with OAFNS. We describe their clinical spectrum, including the report of new features…

0301 basic medicineMaleInheritance Patterns030105 genetics & heredityfrontonasal dysplasiawhole exome sequencingCraniofacial Abnormalities0302 clinical medicinePolymicrogyriaEye AbnormalitiesEar External10. No inequalityChildGenetics (clinical)Exome sequencingwhole genome sequencingThyroid agenesisHypoplasiaDNA-Binding ProteinsPhenotypeChild PreschoolFemaleRespiratory System Abnormalitiesmedicine.medical_specialtyAdolescentQuantitative Trait LociOculoauriculofrontonasal syndrome03 medical and health sciencesExome SequencingGeneticsmedicineHumansGenetic Predisposition to DiseaseFrontonasal dysplasiaGenetic Association StudiesWhole genome sequencingHomeodomain Proteinsbusiness.industryFacial cleftSkullInfant NewbornFaciesInfant030206 dentistrymedicine.diseaseDermatologySpine[SDV.GEN.GH]Life Sciences [q-bio]/Genetics/Human geneticsDysplasiabusinessTomography Spiral ComputedTranscription Factors
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Clinical cardiac assessment in newborns with prenatally diagnosed intrathoracic masses

2018

Abstract Background Congenital space-occupying thoracic malformations and diaphragmatic hernia have in common pulmonary hypoplasia. Our study aims to assess cardiac involvement during post-natal adaptation. Methods A retrospective study was carried out on newborns with prenatally diagnosed intrathoracic mass. Gathering for respiratory distress syndrome (RDS), 35 neonates were compared for clinical course, cardiovascular enzymes, ECG, and ultrasound. Results The analysis revealed a high left heart defect rate in patients with severe RDS, without being influenced by the laterality. Ultrasound or laboratory assessment did not detect altered cardiac dimension or cardiomyopathy. Solely ECG signs…

Prenatal DiagnosiMaleCardiomyopathyCardiovascular abnormalitiesCongenital diaphragmatic herniaCohort StudiesElectrocardiography0302 clinical medicineRetrospective StudiePrenatal DiagnosisRespiratory system abnormalitiesDiaphragmatic hernia030219 obstetrics & reproductive medicineRespiratory distressCardiovascular abnormalitieUltrasoundClinical courselcsh:RJ1-570PrognosisSurvival RateRetrospective studyCardiologyFemaleHumanHeart Defects Congenitalmedicine.medical_specialtyPrognosiRisk AssessmentUltrasonography Prenatal03 medical and health sciencesPulmonary hypoplasia030225 pediatricsInternal medicinemedicineHumansAbnormalities MultipleRetrospective StudiesRespiratory Distress Syndrome Newbornbusiness.industryResearchInfant NewbornRespiratory system abnormalitieCongenital diaphragmatic herniaUltrasonography DopplerRetrospective cohort studylcsh:Pediatricsmedicine.diseaseCohort StudieHernias Diaphragmatic CongenitalbusinessItalian Journal of Pediatrics
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